Research Articles
CRISPR/Cas9: A Genetic Scalpel for Duchenne Muscular Dystrophy
Explore how CRISPR/Cas9 gene editing technology offers revolutionary therapeutic potential for treating Duchenne muscular dystrophy by correcting the underlying genetic mutations.
All-in-One Exosome Engineering: A Revolutionary Approach to Treat Genetic High Cholesterol
Discover how the innovative All-in-One exosome engineering strategy offers new hope for treating familial hypercholesterolemia through precise genetic therapy.
Harnessing Our Viral Heritage: How Ancient Retroviruses Are Revolutionizing Gene Therapy
Discover how syncytins - ancient viral proteins - enable novel possibilities for transducing B cells and achieving well-tolerated in vivo gene transfer.
Taming the Genes: How a Gout Medicine Became a Molecular Master Switch
Discover how scientists engineered oxypurinol-responsive riboswitches from bacterial xanthine aptamers to control gene expression in mammalian cells.
Silencing the Bone Blocker: How a Molecular Brake Holds the Key to Healing Fractures
Discover how scientists are using gene silencing technology to promote bone regeneration by targeting the Smurf1 protein, potentially revolutionizing fracture treatment.
Cutting the Uncuttable: How Gene Therapy and Mathematical Models Are Pioneering an Hepatitis B Cure
Explore how gene therapy using DNA cleavage enzymes combined with mathematical modeling offers new hope for curing chronic Hepatitis B infection.
The Gene Therapy Revolution: Healing Bones with Molecular Blueprints
Breakthrough research in bone regeneration using gene-activated tissue engineering with PEI-condensed BMP-4 plasmid DNA